Рет қаралды 440
ML Bio Solutions: Update on BBP-418 clinical studies for LGMD 2i/R9
• Doug Sproule, MD, ML Bio Solution
SareptaTherapeutics: LGMD2E/R4 and LGMD2B/R2 Gene Therapy
• Louise Rodino-Klapac, PhD, Sarepta Therapeutics
Preliminary Experiences with Atamyo's FKRP Gene Therapy
• John Vissing, MD, University of Copenhagen