mRNA Therapy for Fragile X Syndrome

Dr. Kathryn Whitehead, Associate Professor at Carnegie Mellon University, helped develop the revolutionary science behind the COVID-19 vaccines.
With a 2 year $100,000 grant from FRAXA, her team will now adapt mRNA technology to deliver the missing Fragile X protein, to treat people who have Fragile X syndrome.
The COVID-19 pandemic has fueled the use of messenger RNA (mRNA) as a new class of medicine which has the potential to treat many disorders, including rare genetic disorders like Fragile X syndrome. Recent advances in mRNA technology, including modifications to the mRNA itself along with improvements to the delivery vehicle, have transformed the utility of mRNA as a potential therapy to restore or replace different types of therapeutic proteins.
Learn more about this research grant: www.fraxa.org/...
FRAXA’s mission is to find effective treatments and ultimately a cure for Fragile X syndrome. We directly fund research grants and fellowships at top universities around the world. We partner with biomedical and pharmaceutical companies, large and small, to bridge the gap between research discoveries and actual treatments.
Treatments for Fragile X are likely to help people affected by autism, Alzheimer’s, and other brain disorders.
To learn more about FRAXA's Fragile X syndrome research, to get involved with Fragile X awareness and events or to donate to FRAXA research, visit www.fraxa.org
Let's Connect
Facebook: / fraxaresearch
Instagram: / fraxaresearch
LinkedIn: / fraxa-research-foundation
Twitter: / fraxaresearch
Website: www.fraxa.org

[@ethancallen]

This is amazing, what a time to be alive.

[@universaltruth2025]

You are kidding right …

[@chrisgardner6812]

I knew this from the beginning and why won't our government put this at the fore front of cureing almost all syndromes

[@chrisgardner6812]

I remember asking my biology teacher if we could solve these kind of things back in biology class and I s owed a 96out of 100 on my nys regents exam I wish I pursued biology in college didn't know it would affect me later on in life ty for your determination please help me find a way to help westin you and all the other babies affected by this treatable syndrome

[@neziarushani5959]

Hopefully this Will actualy work.

[@chrisgardner6812]

How can I help??

[@ChildofGod315]

Thank you Jesus. I’m still trusting in God even though I’m having a hard time paying bills and putting groceries in the refrigerator. BUT I STILL TRUST YOU LORD! My faith is what is getting me through my hard situation. I’m struggling to providing for my two autistic children since losing my job over declining the vaccine. I declined due to my pre existing health condition (Lupus) and Heart disease. I was denied my medical/religious exemption from Forsyth Hospital. My husband passed away three years ago, I’m a single mother. I’m all alone. Both of my sons are non verbal so things are more hard on me. Every month I don’t know how we are going to make it through. Every month is a struggle, a battle to not end up on the streets. I’m so depressed and embarrassed by my situation. I’m so ashamed and overwhelmed it’s hard looking in the mirror. BUT because of my faith, God shows up every month and provides. He has even sent strangers to help me, thank you Father. Even as I face homelessness with two young children seemingly every month! I know that God will provide abundantly. Thank you Jesus. I BELIEVE!

[@niharikaram5241]

Hello. I am interested in joining Fraxa Research team, is there any vacancy or position available. I want to contribute in this noble cause of helping the present and future generations

[@FRAXA]

Thank you, Hiharika, we do not have paid openings, but we would be happy for volunteer assistance in raising awareness of Fragile X. Currently we are gearing up for World Fragile X Day which is July 22. worldfragilexday.com/

[@ahmedjowhar9005]

I thank you for your efforts. My son has Fragil X and has hyperactivity. He is 7 years old. Is there an effective medicine?

[@FRAXA]

There are medicines to help with symptoms like hyperactivity. You can find more information at www.fraxa.org/fragile-x-syndrome/#treatment

[@RiaR-yk8fq]

🙏🏽

[@harshmiglani5518]

Is this possible in near future?

[@neziarushani5959]

👍👍

[@neziarushani5959]

How many years ahead are we talking about?

[@FRAXA]

If we only knew the answer to your question ... but it is a road we've not traveled and we just don't know. We are committed to speeding ahead!

[@cazzawazzadingdong5139]

@@FRAXA Thank you.

[@egbertrichards2314]

💐 𝓹𝓻𝓸𝓶𝓸𝓼𝓶