PPMD 2024 Annual Conference: Day 2 - Research Row: Strategies to Restore Dystrophin

  Рет қаралды 178

Parent Project Muscular Dystrophy

Parent Project Muscular Dystrophy

Күн бұрын

Research Row: Strategies to Restore Dystrophin
Annemieke Aartsma-Rus, PhD, University of Leiden (Moderator)
Avidity Biosciences - AOC 1044: Henry Nchienzia, PhD, Avidity Biosciences Biomarin - BMN 351: Peter Velzquez, PhD, BioMarin Pharmaceutical Inc. Dyne Therapeutics - DYNE-251: John Cox, MBA, Dyne Therapeutics
Entrada Therapeutics - ENTR-601-44: Mahasweta Girgenrath, PhD, Entrada Therapeutics
NS Pharma - NS-089 / NS-050: Robert Crozier, PhD, NS Pharma
Pepgen - PGN-EDO51: Bassem Morcos, MD, Pepgen
PTC Therapeutics - Ataluren: Jonathan Blaize, PhD, PTC Therapeutics
Sarepta Therapeutics - SRP-5051: Karin Lucas, PhD, Sarepta Therapeutics Wave Life Sciences - WVE-N531: Angel Angelov, MD, MBA, Wave Life Sciences

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