What you need to know about the Ultragenyx gene therapy trial for Wilson disease

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Wilson Disease Association

Wilson Disease Association

Күн бұрын

Dr. Eric Crombez
Medical Director, Ultragenyx
Dr. Crombez updates us on Ultragenyx’s CYPRUS2+ study and clinical trial, a promising new gene therapy treatment for Wilson disease. You'll learn details about the study, its timeline and potential to restore ATP7B function in the liver. The CYPRUS2+ study continues to enroll adults living with Wilson disease who are currently well-managed on standard of care.
For more information email PatientAdvocacy@Ultragenyx.com
For more information about this trial, visit www.wilsondisease.org under News, Ultragenyx Disease Update August 2023.

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