Natural History Studies & Blood specimen collection @ Boston Children's Hospital; ASOs with n-Lorem

Dr. Chung from Boston Children's Hospital discusses how and why KAND patients should participate in the KAND Natural History Studies (ASCEND and KOALA), and how to provide a blood specimen to her lab.
Then, Dr. Glass from n-Lorem discusses how to engage with ASO treatment and application considerations to n-Lorem.
At the end, Dr. Verden wraps up with a Q & A from the community.