Gene Therapy for Wilson Disease

Wilson disease is a rare genetic disorder that causes excess copper to be stored in the body. The disease is progressive, and if left untreated, can cause liver disease, brain injury, and premature death. Learn how gene therapy may target the cause of disease to slow or stop its progression, along with helpful information on clinical trials, and staying informed.
The subtitling of these videos was funded in part by a donation from Pfizer, Inc.