FA Community Conversations Genetic Therapies Webinar | Recorded August 29, 2024

  Рет қаралды 596

Friedreich's Ataxia Research Alliance

Friedreich's Ataxia Research Alliance

Күн бұрын

Пікірлер: 2
@Baernhardiner
@Baernhardiner 3 ай бұрын
The Brunel University of London has a ongoing Cell an Gene Therapy approach aswell. But it's not on your pipeline chart. Do you have knowledge of it?
@CureFA
@CureFA 2 ай бұрын
Absolutely! We are excited about the work being done at Brunel University of London, and FARA is proud to have provided grant funding for this mouse study: www.curefa.org/funded-grants/therapeutic-activity-of-a-haematopoietic-stem-cell-delivered-tissue-penetrating-peptide-in-a-friedreichs-ataxia-mouse-model/ There are many promising academic research projects underway, and FARA is committed to supporting these efforts. While projects like the one at Brunel are currently in the academic research phase, we're excited to add them to our drug development pipeline if they progress to a company or enter human clinical trials. We're always closely watching these developments and are excited to see how they advance!
Larimar Therapeutics Nomlabofusp Protein Replacement Therapy for Friedreich's Ataxia Webinar
14:53
Friedreich's Ataxia Research Alliance
Рет қаралды 276
Behind the Mystery: Friedreich’s Ataxia
9:21
The Balancing Act
Рет қаралды 99 М.
Enceinte et en Bazard: Les Chroniques du Nettoyage ! 🚽✨
00:21
Two More French
Рет қаралды 42 МЛН
It works #beatbox #tiktok
00:34
BeatboxJCOP
Рет қаралды 41 МЛН
So Cute 🥰 who is better?
00:15
dednahype
Рет қаралды 19 МЛН
Правильный подход к детям
00:18
Beatrise
Рет қаралды 11 МЛН
The First CRISPR Gene Therapy Is Here
12:59
SciShow
Рет қаралды 781 М.
Vitamin D doses
15:17
Dr. John Campbell
Рет қаралды 1,6 МЛН
The Cancer Expert: "This Common Food Is Making Cancer Worse!"
1:37:34
The Diary Of A CEO
Рет қаралды 6 МЛН
Asking The Uncomfortable Questions About Vaccines | Dr. Paul Offit
1:33:34
Simon Sinek's Advice Will Leave You SPEECHLESS 2.0 (MUST WATCH)
20:43
Alpha Leaders
Рет қаралды 1,8 МЛН
Boost Your Bone Density with These 6 Life-Changing Tips
17:18
Talking With Docs
Рет қаралды 800 М.
Astellas Pharma ASP2016 Cardiac Gene Therapy for Friedreich's Ataxia Informational Webinar
40:14
Friedreich's Ataxia Research Alliance
Рет қаралды 234
Enceinte et en Bazard: Les Chroniques du Nettoyage ! 🚽✨
00:21
Two More French
Рет қаралды 42 МЛН